2017. DIA Annual Meeting – Developing the PKUQOL: A long journey to integrate the patients’ voice into phenylketonuria drug development programs

Arnould B. Oral Presentation: Developing the PKUQOL: A long journey to integrate the patients’ voice into phenylketonuria drug development programs. In Session #255: Integrating the Patient’s Voice Across the Development Program of Rare Diseases: Translation Into Meaningful Outcomes. Presented at: DIA Annual 2017 Meeting; June 18-22, 2017; Chicago, IL, USA.